1. From bench to bedside: Improving the clinical safety of GalNAc–siRNA conjugates using seed-pairing destabilization. Issue 12 (23rd June 2022) Authors: Schlegel, Mark K; Janas, Maja M; Jiang, Yongfeng; Barry, Joseph D; Davis, Wendell; Agarwal, Saket; Berman, Daniel; Brown, Christopher R; Castoreno, Adam; LeBlanc, Sarah; Liebow, Abigail; Mayo, Tara; Milstein, Stuart; Nguyen, Tuyen; Shulga-Morskaya, Svetlana; Hyde, Sarah; Schofield, Sally; Szeto, ... Journal: Nucleic acids research Issue: Volume 50:Issue 12(2022) Page Start: 6656 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Phase 1/2 Study of Lumasiran for Treatment of Primary Hyperoxaluria Type 1: A Placebo-Controlled Randomized Clinical Trial. Issue 7 (July 2021) Authors: Frishberg, Yaacov; Deschênes, Georges; Groothoff, Jaap W.; Hulton, Sally-Anne; Magen, Daniella; Harambat, Jérôme; van't Hoff, William G.; Lorch, Ulrike; Milliner, Dawn S.; Lieske, John C.; Haslett, Patrick; Garg, Pushkal P.; Vaishnaw, Akshay K.; Talamudupula, Sandeep; Lu, Jiandong; Habtemariam, B... Other Names: author non-byline.; Bandara Asela author non-byline.; Bowen Jonathan author non-byline.; Chong Wei Li author non-byline.; Coates Simon author non-byline.; De Barr Patrick author non-byline.; De Beer Janine author non-byline.; Gayed Juleen author non-byline.; Hill Timothy author non-byline.; Kota... Journal: Clinical journal of the American Society of Nephrology Issue: Volume 16:Issue 7(2021) Page Start: 1025 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗