1. Achieving Life Milestones in Duchenne/Becker Muscular Dystrophy: A Retrospective Analysis. Issue 4 (August 2021) Authors: Donaldson, Andrew; Guntrum, Debra; Ciafaloni, Emma; Statland, Jeffrey Journal: Neurology Issue: Volume 11:Issue 4(2021) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Nusinersen for older patients with spinal muscular atrophy: A real‐world clinical setting experience. Issue 2 (13th December 2019) Authors: Veerapandiyan, Aravindhan; Eichinger, Katy; Guntrum, Debra; Kwon, Jennifer; Baker, Lindsay; Collins, Erin; Ciafaloni, Emma Journal: Muscle & nerve Issue: Volume 61:Issue 2(2020) Page Start: 222 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗