1. Dynamics of genetically engineered hematopoietic stem and progenitor cells after autologous transplantation in humans. (November 2018) Authors: Scala, Serena; Basso-Ricci, Luca; Dionisio, Francesca; Pellin, Danilo; Giannelli, Stefania; Salerio, Federica; Leonardelli, Lorena; Cicalese, Maria; Ferrua, Francesca; Aiuti, Alessandro; Biasco, Luca Journal: Nature medicine Issue: Volume 24:Number 11(2018) Page Start: 1683 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Follicular helper T cell signature of replicative exhaustion, apoptosis, and senescence in common variable immunodeficiency. Issue 7 (29th May 2022) Authors: Milardi, Giulia; Di Lorenzo, Biagio; Gerosa, Jolanda; Barzaghi, Federica; Di Matteo, Gigliola; Omrani, Maryam; Jofra, Tatiana; Merelli, Ivan; Barcella, Matteo; Filippini, Matteo; Conti, Anastasia; Ferrua, Francesca; Pozzo Giuffrida, Francesco; Dionisio, Francesca; Rovere‐Querini, Patrizia; Markte... Journal: European journal of immunology Issue: Volume 52:Issue 7(2022) Page Start: 1171 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Gene Modification and Three-Dimensional Scaffolds as Novel Tools to Allow the Use of Postnatal Thymic Epithelial Cells for Thymus Regeneration Approaches. (29th May 2019) Authors: Bortolomai, Ileana; Sandri, Monica; Draghici, Elena; Fontana, Elena; Campodoni, Elisabetta; Marcovecchio, Genni Enza; Ferrua, Francesca; Perani, Laura; Spinelli, Antonello; Canu, Tamara; Catucci, Marco; Di Tomaso, Tiziano; Sergi Sergi, Lucia; Esposito, Antonio; Lombardo, Angelo; Naldini, Luigi; T... Journal: Stem cells translational medicine Issue: Volume 8:Number 10(2019) Page Start: 1107 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. Gene Modification and Three‐Dimensional Scaffolds as Novel Tools to Allow the Use of Postnatal Thymic Epithelial Cells for Thymus Regeneration Approaches. (29th May 2019) Authors: Bortolomai, Ileana; Sandri, Monica; Draghici, Elena; Fontana, Elena; Campodoni, Elisabetta; Marcovecchio, Genni Enza; Ferrua, Francesca; Perani, Laura; Spinelli, Antonello; Canu, Tamara; Catucci, Marco; Di Tomaso, Tiziano; Sergi Sergi, Lucia; Esposito, Antonio; Lombardo, Angelo; Naldini, Luigi; T... Journal: Stem cells translational medicine Issue: Volume 8:Number 10(2019) Page Start: 1107 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access. Issue 10322 (22nd January 2022) Authors: Fumagalli, Francesca; Calbi, Valeria; Natali Sora, Maria Grazia; Sessa, Maria; Baldoli, Cristina; Rancoita, Paola Maria V; Ciotti, Francesca; Sarzana, Marina; Fraschini, Maddalena; Zambon, Alberto Andrea; Acquati, Serena; Redaelli, Daniela; Attanasio, Vanessa; Miglietta, Simona; De Mattia, Fabiol... Journal: Lancet Issue: Volume 399:Issue 10322(2022) Page Start: 372 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
6. Lentiviral haemopoietic stem/progenitor cell gene therapy for treatment of Wiskott-Aldrich syndrome: interim results of a non-randomised, open-label, phase 1/2 clinical study. Issue 5 (May 2019) Authors: Ferrua, Francesca; Cicalese, Maria Pia; Galimberti, Stefania; Giannelli, Stefania; Dionisio, Francesca; Barzaghi, Federica; Migliavacca, Maddalena; Bernardo, Maria Ester; Calbi, Valeria; Assanelli, Andrea Angelo; Facchini, Marcella; Fossati, Claudia; Albertazzi, Elena; Scaramuzza, Samantha; Brigi... Journal: Lancet Issue: Volume 6:Issue 5(2019) Page Start: e239 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
7. Modeling, optimization, and comparable efficacy of T cell and hematopoietic stem cell gene editing for treating hyper‐IgM syndrome. Issue 3 (21st January 2021) Authors: Vavassori, Valentina; Mercuri, Elisabetta; Marcovecchio, Genni E; Castiello, Maria C; Schiroli, Giulia; Albano, Luisa; Margulies, Carrie; Buquicchio, Frank; Fontana, Elena; Beretta, Stefano; Merelli, Ivan; Cappelleri, Andrea; Rancoita, Paola MV; Lougaris, Vassilios; Plebani, Alessandro; Kanariou,... Journal: EMBO molecular medicine Issue: Volume 13:Issue 3(2021) Page Start: n/a Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
8. Successful Treatment With Ledipasvir/Sofosbuvir in an Infant With Severe Combined Immunodeficiency Caused by Adenosine Deaminase Deficiency With HCV Allowed Gene Therapy with Strimvelis. Issue 6 (13th November 2018) Authors: Tucci, Francesca; Calbi, Valeria; Barzaghi, Federica; Migliavacca, Maddalena; Ferrua, Francesca; Bernardo, Maria Ester; Canarutto, Daniele; Consiglieri, Giulia; Recupero, Salvatore; Calzatini, Francesco; Gabaldo, Michela; Lucano, Caterina; Casiraghi, Miriam; Darin, Silvia; Dionisio, Francesca; Ma... Journal: Hepatology Issue: Volume 68:Issue 6(2018) Page Start: 2434 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
9. Third cranial nerve palsy in an 88-year-old man after SARS-CoV-2 mRNA vaccination: change of injection site and type of vaccine resulted in an uneventful second dose with humoral immune response. Issue 2 (8th February 2022) Authors: Cicalese, Maria Pia; Ferrua, Francesca; Barzaghi, Federica; Cerri, Federica; Moro, Matteo; Aiuti, Alessandro; Silvani, Paolo Journal: BMJ case reports Issue: Volume 15:Issue 2(2022) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
10. Wiskott–Aldrich syndrome: Oral findings and microbiota in children and review of the literature. Issue 1 (24th February 2022) Authors: Lucchese, Alessandra; Cenciarelli, Sabina; Manuelli, Maurizio; Marcolina, Marta; Barzaghi, Federica; Calbi, Valeria; Migliavacca, Maddalena; Bernardo, Maria Ester; Tucci, Francesca; Gallo, Vera; Fraschetta, Federico; Darin, Silvia; Casiraghi, Miriam; Aiuti, Alessandro; Ferrua, Francesca; Cicalese... Journal: Clinical and experimental dental research Issue: Volume 8:Issue 1(2022) Page Start: 28 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗