1. Biochemical response to substrate reduction therapy versus enzyme replacement therapy in Gaucher disease type 1 patients. Issue 1 (December 2016) Authors: Smid, Bouwien; Ferraz, Maria; Verhoek, Marri; Mirzaian, Mina; Wisse, Patrick; Overkleeft, Herman; Hollak, Carla; Aerts, Johannes Journal: Orphanet journal of rare diseases Issue: Volume 11:Issue 1(2016) Page Start: 1 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗