1. An overview of the efficacy and safety of deferiprone in paediatric patients with congenital haemoglobinopathies and chronic iron overload. (3rd April 2019) Authors: Ceci, Adriana; Conte, Rosa; Didio, Antonella; Bonifazi, Donato; Felisi, Mariagrazia; Giannuzzi, Viviana; Bonifazi, Fedele Journal: Expert opinion on orphan drugs Issue: Volume 7:Number 4(2019) Page Start: 181 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Evaluation of the efficacy and safety of deferiprone compared with deferasirox in paediatric patients with transfusion-dependent haemoglobinopathies (DEEP-2): a multicentre, randomised, open-label, non-inferiority, phase 3 trial. Issue 6 (June 2020) Authors: Maggio, Aurelio; Kattamis, Antonis; Felisi, Mariagrazia; Reggiardo, Giorgio; El-Beshlawy, Amal; Bejaoui, Mohamed; Sherief, Laila; Christou, Soteroula; Cosmi, Carlo; Della Pasqua, Oscar; Del Vecchio, Giovanni Carlo; Filosa, Aldo; Cuccia, Liana; Hassab, Hoda; Kreka, Manika; Origa, Raffaella; Putti,... Journal: Lancet Issue: Volume 7:Issue 6(2020) Page Start: e469 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Failures to further developing orphan medicinal products after designation granted in Europe: an analysis of marketing authorisation failures and abandoned drugs. Issue 9 (11th September 2017) Authors: Giannuzzi, Viviana; Landi, Annalisa; Bosone, Enrico; Giannuzzi, Floriana; Nicotri, Stefano; Torrent-Farnell, Josep; Bonifazi, Fedele; Felisi, Mariagrazia; Bonifazi, Donato; Ceci, Adriana Journal: BMJ open Issue: Volume 7:Issue 9(2017) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. Non-inferiority double-blind randomised controlled trial comparing gabapentin versus tramadol for the treatment of chronic neuropathic or mixed pain in children and adolescents: the GABA-1 trial—a study protocol. Issue 2 (20th February 2019) Authors: Kaguelidou, Florentia; Le Roux, Enora; Mangiarini, Laura; Lundin, Rebecca; de Leeuw, Thomas G; Della Pasqua, Oscar; Felisi, Mariagrazia; Bonifazi, Donato; Tibboel, Dick; Ceci, Adriana; de Wildt, Saskia N; Alberti, Corinne Other Names: author non-byline.; Bali Donjeta author non-byline.; Hoxha Alketa author non-byline.; Kola Ermira author non-byline.; Talvik Inga author non-byline.; Andrieu-Galien Juliette author non-byline.; Greco Celine author non-byline.; Annequin Daniel author non-byline.; Avez-couturier Justine author non... Journal: BMJ open Issue: Volume 9:Issue 2(2019) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. Overview of the European post‐authorisation study register post‐authorization studies performed in Europe from September 2010 to December 2018. Issue 6 (11th February 2022) Authors: Sultana, Janet; Crisafulli, Salvatore; Almas, Mariana; Antonazzo, Ippazio Cosimo; Baan, Esme; Bartolini, Claudia; Bertuccio, Maria Paola; Bonifazi, Fedele; Capuano, Annalisa; Didio, Antonella; Ehrenstein, Vera; Felisi, Mariagrazia; Ferrajolo, Carmen; Fontana, Andrea; Francisca, Remy; Fourrier‐Reg... Journal: Pharmacoepidemiology and drug safety Issue: Volume 31:Issue 6(2022) Page Start: 689 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
6. Pattern of complications and burden of disease in patients affected by beta thalassemia major. (3rd August 2017) Authors: Bonifazi, Fedele; Conte, Rosa; Baiardi, Paola; Bonifazi, Donato; Felisi, Mariagrazia; Giordano, Paola; Giannuzzi, Viviana; Iacono, Angela; Padula, Rosa; Pepe, Alessia; Caterina Putti, Maria; Ruggieri, Lucia; Carlo Del Vecchio, Giovanni; Filosa, Aldo; Maggio, Aurelio; Ceci, Adriana Journal: Current medical research and opinion Issue: Volume 33:Number 8(2017) Page Start: 1525 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
7. Presence and activities of clinical research coordinators at Italian Health Care Institutions: A national cross-sectional survey. Issue 1 (28th October 2022) Authors: Caminiti, Caterina; Maglietta, Giuseppe; Frau, Ileana; Peruzzotti, Giulia; Felisi, Mariagrazia; van Dijk, Antoinette Journal: Journal of clinical and translational science Issue: Volume 6:Issue 1(2022) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
8. The Italian multiregional thalassemia registry: Centers characteristics, services, and patients' population†. Issue 7 (8th August 2016) Authors: Conte, Rosa; Ruggieri, Lucia; Gambino, Arianna; Bartoloni, Franco; Baiardi, Paola; Bonifazi, Donato; Bonifazi, Fedele; Felisi, Mariagrazia; Giannuzzi, Viviana; Padula, Rosa; Pepe, Alessia; Putti, Maria Caterina; Del Vecchio, Giovanni Carlo; Maggio, Aurelio; Filosa, Aldo; Iacono, Angela; Mangiarin... Journal: Hematology Issue: Volume 21:Issue 7(2016) Page Start: 415 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
9. The Management of Iron Chelation Therapy: Preliminary Data from a National Registry of Thalassaemic Patients. (5th June 2011) Authors: Ceci, Adriana; Mangiarini, Laura; Felisi, Mariagrazia; Bartoloni, Franco; Ciancio, Angela; Capra, Marcello; D'Ascola, Domenico; Cianciulli, Paolo; Filosa, Aldo Other Names: Kilinç Yurdanur Academic Editor. Journal: Anemia Issue: Volume 2011(2011) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗