1. Disease correction in mucopolysaccharidosis type IIIB mice by intraparenchymal or cisternal delivery of a capsid modified AAV8 codon-optimized NAGLU vector. Issue 3 (23rd August 2022) Authors: Rouse, Courtney J; Hawkins, Kimberley; Kabbej, Nadia; Dalugdug, Justin; Kunta, Aishwarya; Kim, Mi-Jung; Someya, Shinichi; Herbst, Zachary; Gelb, Michael; Dinelli, Isabella; Butterworth, Elizabeth; Falk, Darin J; Rosenkrantz, Erinn; Elmohd, Hamza; Khaledi, Hamid; Mowafy, Samar; Ashby, Frederick; H... Journal: Human molecular genetics Issue: Volume 32:Issue 3(2023) Page Start: 417 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗