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Author/Creator Elfring, Gary

1. Ataluren in patients with nonsense mutation Duchenne muscular dystrophy (ACT DMD): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial. Issue 10101 (23rd September 2017)

Authors:
McDonald, Craig M; Campbell, Craig; Torricelli, Ricardo Erazo; Finkel, Richard S; Flanigan, Kevin M; Goemans, Nathalie; Heydemann, Peter; Kaminska, Anna; Kirschner, Janbernd; Muntoni, Francesco; Osorio, Andrés Nascimento; Schara, Ulrike; Sejersen, Thomas; Shieh, Perry B; Sweeney, H Lee; Topaloglu...
Journal:
Lancet
Issue:
Volume 390:Issue 10101(2017)
Page Start:
1489
Record Type:
Journal Article
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3. Deflazacort versus prednisone/prednisolone for maintaining motor function and delaying loss of ambulation: A post HOC analysis from the ACT DMD trial. Issue 5 (27th September 2018)

Authors:
Shieh, Perry B.; M intosh, Joseph; Jin, Fengbin; Souza, Marcio; Elfring, Gary; Narayanan, Siva; Trifillis, Panayiota; Peltz, Stuart W.; M donald, Craig M.; Darras, Basil T.
Journal:
Muscle & nerve
Issue:
Volume 58:Issue 5(2018)
Page Start:
639
Record Type:
Journal Article
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4. Deflazacort vs prednisone treatment for Duchenne muscular dystrophy: A meta‐analysis of disease progression rates in recent multicenter clinical trials. Issue 1 (7th November 2019)

Authors:
McDonald, Craig M.; Sajeev, Gautam; Yao, Zhiwen; McDonnell, Erin; Elfring, Gary; Souza, Marcio; Peltz, Stuart W.; Darras, Basil T.; Shieh, Perry B.; Cox, David A.; Landry, John; Signorovitch, James
Journal:
Muscle & nerve
Issue:
Volume 61:Issue 1(2020)
Page Start:
26
Record Type:
Journal Article
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6. Phase 1 Study of Safety, Tolerability, and Pharmacokinetics of PTC299, an Inhibitor of Stress‐Regulated Protein Translation. Issue 4 (2nd February 2016)

Authors:
Weetall, Marla; Davis, Thomas; Elfring, Gary; Northcutt, Valerie; Cao, Liangxian; Moon, Young‐Choon; Riebling, Peter; Dali, Mandar; Hirawat, Samit; Babiak, John; Colacino, Joseph; Almstead, Neil; Spiegel, Robert; Peltz, Stuart W.
Journal:
Clinical pharmacology in drug development
Issue:
Volume 5:Issue 4(2016:Jul./Aug.)
Page Start:
296
Record Type:
Journal Article
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7. The 6‐minute walk test and other clinical endpoints in duchenne muscular dystrophy: Reliability, concurrent validity, and minimal clinically important differences from a multicenter study. Issue 3 (17th July 2013)

Authors:
McDonald, Craig M.; Henricson, Erik K.; Abresch, R. Ted; Florence, Julaine; Eagle, Michelle; Gappmaier, Eduard; Glanzman, Allan M.; Spiegel, Robert; Barth, Jay; Elfring, Gary; Reha, Allen; Peltz, Stuart W.
Journal:
Muscle & nerve
Issue:
Volume 48:Issue 3(2013:Sep.)
Page Start:
357
Record Type:
Journal Article
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8. THE 6‐minute walk test and other endpoints in Duchenne muscular dystrophy: Longitudinal natural history observations over 48 weeks from a multicenter study. Issue 3 (26th June 2013)

Authors:
Mcdonald, Craig M.; Henricson, Erik K.; Abresch, R. Ted; Florence, Julaine M.; Eagle, Michelle; Gappmaier, Eduard; Glanzman, Allan M.; Spiegel, Robert; Barth, Jay; Elfring, Gary; Reha, Allen; Peltz, Stuart
Journal:
Muscle & nerve
Issue:
Volume 48:Issue 3(2013:Sep.)
Page Start:
343
Record Type:
Journal Article
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Available online (eLD content is only available in our Reading Rooms) ↗