1. A.06 Ataluren: an overview of clinical trial results in nonsense mutation Duchenne Muscular Dystrophy (nmDMD). (17th June 2016) Authors: McDonald, CM; Bushby, K; Tulinius, M; Finkel, R; Topaloglu, H; Day, JW; Flanigan, K; Lowes, L; Eagle, M; Luo, X; Elfring, G; Kroger, H; Riebling, P; Ong, T; Spiegel, R; Peltz, SW Journal: Canadian journal of neurological sciences Issue: Volume 43(2016)Supplement 2 Page Start: S8 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. D.08 ACT DMD (Ataluren Confirmatory Trial in Duchenne Muscular Dystrophy): effect of Ataluren on timed function tests (TFT) in nonsense mutation (nm) DMD. (17th June 2016) Authors: Goemans, N; Campbell, C; McDonald, CM; Voit, T; Luo, X; Elfring, G; Kroger, H; Riebling, P; Ong, T; Spiegel, R; Peltz, SW; Bushby, K Journal: Canadian journal of neurological sciences Issue: Volume 43(2016)Supplement 2 Page Start: S15 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗