1. 062 A novel scoring system for the respiratory health of children with spinal muscular atrophy type 1. (December 2018) Authors: Robinson, V; Edel, L; Grime, C; Chan, E Journal: Archives of disease in childhood Issue: Volume 103(2018)Supplement 2 Page Start: A25 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. B1.3 The development and evaluation of a physiotherapy led respiratory outpatient clinic at great ormond street hospital (gosh). (4th October 2017) Authors: Hill, L; Edel, L Journal: Archives of disease in childhood Issue: Volume 102(2017)Supplement 3 Page Start: A3 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. G299 Nusinersen (spinraza) is the first drug approved for spinal muscular atrophy (sma): initial experience in patients with sma type 1 treated in the expanded access program (eap). (12th March 2018) Authors: Scoto, M; Main, M; Munot, P; Edel, L; Abel, F; Chan, E; Manzur, A; Muntoni, F Journal: Archives of disease in childhood Issue: Volume 103(2018)Supplement 1 Page Start: A122 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗