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2. NFB-09. ENROLLMENT AND CLINICAL CHARACTERISTICS OF NEWLY DIAGNOSED, NEUROFIBROMATOSIS TYPE 1 ASSOCIATED OPTIC PATHWAY GLIOMA (NF1-OPG): PRELIMINARY RESULTS FROM AN INTERNATIONAL MULTI-CENTER NATURAL HISTORY STUDY. (4th December 2020)

5. Study design and baseline characteristics for the reflect gene therapy trial ofm.11778g>A/ND4-LHON. Issue 1 (15th November 2022)