1. Efficacy and safety of cyclic pyranopterin monophosphate substitution in severe molybdenum cofactor deficiency type A: a prospective cohort study. Issue 10007 (14th November 2015) Authors: Schwahn, Bernd C; Van Spronsen, Francjan J; Belaidi, Abdel A; Bowhay, Stephen; Christodoulou, John; Derks, Terry G; Hennermann, Julia B; Jameson, Elisabeth; König, Kai; McGregor, Tracy L; Font-Montgomery, Esperanza; Santamaria-Araujo, José A; Santra, Saikat; Vaidya, Mamta; Vierzig, Anne; Wassmer,... Journal: Lancet Issue: Volume 386:Issue 10007(2015) Page Start: 1955 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗