1. 4CPS-131 Effectiveness of nusinersen in paediatric patients SMA1 and SMA2. (24th March 2020) Authors: Ortenzi, GB; Palmas, G; Andresciani, E; Garzone, AMF; Berardi, MA; Siliquini, S; Porfiri, L; Demeo, MS; Guglielmi, S; Polidori, C; Pompilio, A Journal: European journal of hospital pharmacy Issue: Volume 27(2020)Supplement 1 Page Start: A109 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗