1. Liver‐directed gene therapy for ornithine aminotransferase deficiency. Issue 4 (17th January 2023) Authors: Boffa, Iolanda; Polishchuk, Elena; De Stefano, Lucia; Dell'Aquila, Fabio; Nusco, Edoardo; Marrocco, Elena; Audano, Matteo; Pedretti, Silvia; Caterino, Marianna; Bellezza, Ilaria; Ruoppolo, Margherita; Mitro, Nico; Cellini, Barbara; Auricchio, Alberto; Brunetti‐Pierri, Nicola Journal: EMBO molecular medicine Issue: Volume 15:Issue 4(2023) Page Start: n/a Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗