1. Enzyme replacement therapy with taliglucerase alfa: 36‐month safety and efficacy results in adult patients with Gaucher disease previously treated with imiglucerase. Issue 7 (18th May 2016) Authors: Pastores, Gregory M.; Shankar, Suma P.; Petakov, Milan; Giraldo, Pilar; Rosenbaum, Hanna; Amato, Dominick J.; Szer, Jeffrey; Chertkoff, Raul; Brill‐Almon, Einat; Zimran, Ari Journal: American journal of hematology Issue: Volume 91:Issue 7(2016:Jul.) Page Start: 661 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. FP805PROGRESSION OF NEPHROPATHY IN FABRY PATIENTS RECEIVING ENZYME REPLACEMENT THERAPY (ERT); RELATION TO ANTI-DRUG ANTIBODY (ADA) STATUS AND PROTEINURIA. (28th May 2018) Authors: Warnock, David; Alon, Sari; Chertkoff, Raul; Brill-Almon, Einat Journal: Nephrology dialysis transplantation Issue: Volume 33(2018)Supplement 1 Page Start: i634 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Improvement in bone marrow infiltration in patients with type I Gaucher disease treated with taliglucerase alfa. Issue 6 (31st July 2018) Authors: Zimran, Ari; Dinur, Tama; Revel‐Vilk, Shoshana; Akkerman, Eric M.; van Dussen, Laura; Hollak, Carla E. M.; Maayan, Hannah; Altarescu, Gheona; Chertkoff, Raul; Maas, Mario Journal: Journal of inherited metabolic disease Issue: Volume 41:Issue 6(2018) Page Start: 1259 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. Long‐term efficacy and safety results of taliglucerase alfa up to 36 months in adult treatment‐naïve patients with Gaucher disease. Issue 7 (24th April 2016) Authors: Zimran, Ari; Durán, Gloria; Mehta, Atul; Giraldo, Pilar; Rosenbaum, Hanna; Giona, Fiorina; Amato, Dominick J.; Petakov, Milan; Muñoz, Eduardo Terreros; Solorio‐Meza, Sergio Eduardo; Cooper, Peter A.; Varughese, Sheeba; Chertkoff, Raul; Brill‐Almon, Einat Journal: American journal of hematology Issue: Volume 91:Issue 7(2016:Jul.) Page Start: 656 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. MO034A SUBGROUP ANALYSIS OF FEMALE PATIENTS IN A PHASE 3 OPEN-LABEL STUDY TO ASSESS THE SAFETY AND EFFICACY OF PEGUNIGALSIDASE ALFA IN PATIENTS WITH FABRY DISEASE PREVIOUSLY TREATED WITH AGALSIDASE ALFA. (29th May 2021) Authors: Hughes, Derralynn; Dostalova, Gabriela; Nicholls, Kathy; West, Michael; Tã¸ndel, Camilla; Jovanovic, Ana; Castellano, Pilar Giraldo; Vujkovac, Bojan; Geberhiwot, Tarekegn; Almon, Einat; Alon, Sari; Szlaifer, Mali; Chertkoff, Raul; Linhart, Ales Journal: Nephrology dialysis transplantation Issue: Volume 36(2021)Supplement 1 Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
6. Novel Orally Administered Recombinant Anti-TNF Alpha Fusion Protein for the Treatment of Ulcerative Colitis: Results From a Phase 2a Clinical Trial. Issue 2 (February 2021) Authors: Almon, Einat; Shaaltiel, Yoseph; Sbeit, Wisam; Fich, Alex; Schwartz, Doron; Waterman, Mattitiahu; Szlaifer, Mali; Reuveni, Hadar; Amit-Cohen, Bat-chen; Alon, Sari; Chertkoff, Raul; Paz, Alona; Ilan, Yaron Journal: Journal of clinical gastroenterology Issue: Volume 55:Issue 2(2021) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
7. Pegunigalsidase alfa, a novel PEGylated enzyme replacement therapy for Fabry disease, provides sustained plasma concentrations and favorable pharmacodynamics: A 1‐year Phase 1/2 clinical trial. Issue 3 (8th April 2019) Authors: Schiffmann, Raphael; Goker‐Alpan, Ozlem; Holida, Myrl; Giraldo, Pilar; Barisoni, Laura; Colvin, Robert B.; Jennette, Charles J.; Maegawa, Gustavo; Boyadjiev, Simeon A.; Gonzalez, Derlis; Nicholls, Kathy; Tuffaha, Ahmad; Atta, Mohamed G.; Rup, Bonita; Charney, Martha R.; Paz, Alona; Szlaifer, Mali... Journal: Journal of inherited metabolic disease Issue: Volume 42:Issue 3(2019) Page Start: 534 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗