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4. Preclinical evaluation of RNAi as a treatment for transthyretin-mediated amyloidosis. (2nd April 2016)

5. RNAi‐mediated reduction of hepatic Tmprss6 diminishes anemia and secondary iron overload in a splenectomized mouse model of β‐thalassemia intermedia. Issue 6 (23rd March 2018)