1. An observational study of functional abilities in infants, children, and adults with type 1 SMA. (21st August 2018) Authors: Pane, Marika; Palermo, Concetta; Messina, Sonia; Sansone, Valeria A.; Bruno, Claudio; Catteruccia, Michela; Sframeli, Maria; Albamonte, Emilio; Pedemonte, Marina; D'Amico, Adele; Brigati, Giorgia; de Sanctis, Roberto; Coratti, Giorgia; Lucibello, Simona; Bertini, Enrico; Vita, Giuseppe; Danilo Ti... Journal: Neurology Issue: Volume 91:Number 8(2018) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Nusinersen in type 1 spinal muscular atrophy: Twelve‐month real‐world data. Issue 3 (8th July 2019) Authors: Pane, Marika; Coratti, Giorgia; Sansone, Valeria A.; Messina, Sonia; Bruno, Claudio; Catteruccia, Michela; Sframeli, Maria; Albamonte, Emilio; Pedemonte, Marina; D'Amico, Adele; Bravetti, Chiara; Berti, Beatrice; Brigati, Giorgia; Tacchetti, Paola; Salmin, Francesca; de Sanctis, Roberto; Lucibell... Journal: Annals of neurology Issue: Volume 86:Issue 3(2019) Page Start: 443 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Type I SMA "new natural history": long‐term data in nusinersen‐treated patients. Issue 3 (6th February 2021) Authors: Pane, Marika; Coratti, Giorgia; Sansone, Valeria A.; Messina, Sonia; Catteruccia, Michela; Bruno, Claudio; Sframeli, Maria; Albamonte, Emilio; Pedemonte, Marina; D'Amico, Adele; Bravetti, Chiara; Berti, Beatrice; Palermo, Concetta; Leone, Daniela; Brigati, Giorgia; Tacchetti, Paola; Salmin, Franc... Journal: Annals of clinical and translational neurology Issue: Volume 8:Issue 3(2021) Page Start: 548 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗