1. Arginine butyrate: a therapeutic candidate for Duchenne muscular dystrophy. Issue 6 (21st February 2013) Authors: Vianello, Sara; Yu, Hua; Voisin, Vincent; Haddad, Hafedh; He, Xun; Foutz, Arthur S.; Sebrié, Catherine; Gillet, Brigitte; Roulot, Morgane; Fougerousse, Françoise; Perronnet, Caroline; Vaillend, Cyrille; Matecki, Stefan; Escolar, Diana; Bossi, Laura; Israël, Maurice; de la Porte, Sabine Journal: FASEB journal Issue: Volume 27:Issue 6(2013) Page Start: 2256 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Erratum to: An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A. Issue 1 (December 2016) Authors: Attarian, Shahram; Vallat, Jean-Michel; Magy, Laurent; Funalot, Benoît; Gonnaud, Pierre-Marie; Lacour, Arnaud; Péréon, Yann; Dubourg, Odile; Pouget, Jean; Micallef, Joëlle; Franques, Jérôme; Lefebvre, Marie-Noëlle; Ghorab, Karima; Al-Moussawi, Mahmoud; Tiffreau, Vincent; Preudhomme, Marguerite; M... Journal: Orphanet journal of rare diseases Issue: Volume 11:Issue 1(2016) Page Start: 1 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗