1. A novel ABCC6 haplotype is associated with azathioprine drug response in myasthenia gravis. Issue 2 (February 2017) Authors: Colleoni, Lara; Galbardi, Barbara; Barzago, Claudia; Bonanno, Silvia; Franzi, Sara; Frangiamore, Rita; Camera, Giorgia; Foti, Maria; Biancolini, Donatella; Canioni, Eleonora; Maggi, Lorenzo; Antozzi, Carlo; Mantegazza, Renato; Bernasconi, Pia; Kapetis, Dimos Journal: Pharmaocogenetics and genomics Issue: Volume 27:Issue 2(2017:Feb.) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Adults with spinal muscular atrophy: a large-scale natural history study shows gender effect on disease. Issue 12 (11th October 2022) Authors: Maggi, Lorenzo; Bello, Luca; Bonanno, Silvia; Govoni, Alessandra; Caponnetto, Claudia; Passamano, Luigia; Grandis, Marina; Trojsi, Francesca; Cerri, Federica; Gardani, Alice; Ferraro, Manfredi; Gadaleta, Giulio; Zangaro, Vittoria; Caumo, Luca; Maioli, Mariantonietta; Tanel, Raffaella; Saccani, El... Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 93:Issue 12(2022) Page Start: 1253 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Amifampridine phosphate in the treatment of muscle-specific kinase myasthenia gravis: a phase IIb, randomized, double-blind, placebo-controlled, double crossover study. (December 2018) Authors: Bonanno, Silvia; Pasanisi, Maria Barbara; Frangiamore, Rita; Maggi, Lorenzo; Antozzi, Carlo; Andreetta, Francesca; Campanella, Angela; Brenna, Greta; Cottini, Lorenzo; Mantegazza, Renato Journal: SAGE open medicine Issue: Volume 6(2018) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. Hyperexcitability in Cultured Cortical Neuron Networks from the G93A-SOD1 Amyotrophic Lateral Sclerosis Model Mouse and its Molecular Correlates. (15th September 2019) Authors: Marcuzzo, Stefania; Terragni, Benedetta; Bonanno, Silvia; Isaia, Davide; Cavalcante, Paola; Cappelletti, Cristina; Ciusani, Emilio; Rizzo, Ambra; Regalia, Giulia; Yoshimura, Natsue; Ugolini, Giovanni Stefano; Rasponi, Marco; Bechi, Giulia; Mantegazza, Massimo; Mantegazza, Renato; Bernasconi, Pia;... Journal: Neuroscience Issue: Volume 416(2019) Page Start: 88 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. MicroRNA signature associated with treatment response in myasthenia gravis: A further step towards precision medicine. (October 2019) Authors: Cavalcante, Paola; Mizrachi, Tehila; Barzago, Claudia; Scandiffio, Letizia; Bortone, Federica; Bonanno, Silvia; Frangiamore, Rita; Mantegazza, Renato; Bernasconi, Pia; Brenner, Talma; Vaknin-Dembinsky, Adi; Antozzi, Carlo Journal: Pharmacological research Issue: Volume 148(2019) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
6. Nusinersen safety and effects on motor function in adult spinal muscular atrophy type 2 and 3. Issue 11 (11th September 2020) Authors: Maggi, Lorenzo; Bello, Luca; Bonanno, Silvia; Govoni, Alessandra; Caponnetto, Claudia; Passamano, Luigia; Grandis, Marina; Trojsi, Francesca; Cerri, Federica; Ferraro, Manfredi; Bozzoni, Virginia; Caumo, Luca; Piras, Rachele; Tanel, Raffaella; Saccani, Elena; Meneri, Megi; Vacchiano, Veria; Ricci... Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 91:Issue 11(2020) Page Start: 1166 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
7. Revealing the involvement of miR-376a, miR-432 and miR-451a in infantile ascending hereditary spastic paralysis by microRNA profiling in iPSCs. Issue 1 (2019) Authors: Marcuzzo, tefania; Bonanno, Silvia; Barzago, Claudia; D'Alessandro, Sara; Cavalcante, Paola; Galbardi, Barbara Journal: Journal of translational science Issue: Volume 5:Issue 1(2019) Page Start: Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
8. Safety, efficacy, and tolerability of efgartigimod in patients with generalised myasthenia gravis (ADAPT): a multicentre, randomised, placebo-controlled, phase 3 trial. Issue 7 (July 2021) Authors: Howard, James F; Bril, Vera; Vu, Tuan; Karam, Chafic; Peric, Stojan; Margania, Temur; Murai, Hiroyuki; Bilinska, Malgorzata; Shakarishvili, Roman; Smilowski, Marek; Guglietta, Antonio; Ulrichts, Peter; Vangeneugden, Tony; Utsugisawa, Kimiaki; Verschuuren, Jan; Mantegazza, Renato; De Bleeker, Jan;... Journal: Lancet neurology Issue: Volume 20:Issue 7(2021) Page Start: 526 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
9. Safety, efficacy, and tolerability of efgartigimod in patients with generalised myasthenia gravis (ADAPT): a multicentre, randomised, placebo-controlled, phase 3 trial. Issue 7 (July 2021) Authors: Howard, James F; Bril, Vera; Vu, Tuan; Karam, Chafic; Peric, Stojan; Margania, Temur; Murai, Hiroyuki; Bilinska, Malgorzata; Shakarishvili, Roman; Smilowski, Marek; Guglietta, Antonio; Ulrichts, Peter; Vangeneugden, Tony; Utsugisawa, Kimiaki; Verschuuren, Jan; Mantegazza, Renato; De Bleecker, Jan... Journal: Lancet neurology Issue: Volume 20:Issue 7(2021) Page Start: 526 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗