1. L4 Sustained and strong HTT silencing by AAV5-miHTT as therapy for huntington's disease. (13th September 2016) Authors: Evers, Melvin; Miniarikova, Jana; Blits, Bas; Spronck, Lisa; Brouwers, Cynthia; Déglon, Nicole; Motlik, Jan; Bankiewicz, Krystof; Southwell, Amber; Haan, Martin de; Richard, Charles; Petry, Harald; Konstantinova, Pavlina Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 87(2016)Supplement 1 Page Start: A91 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. L5 Pre-clinical evaluation of aav5-mihtt gene therapy of huntington's disease in rodents. (13th September 2016) Authors: Miniarikova, Jana; Zanella, Ilaria; Blits, Bas; Evers, Melvin; Zimmer, Virginie; Spoerl, Alexia; Southwell, Amber; Hayden, Michael; Deventer, Sander van; Deglon, Nicole; Petry, Harald; Konstantinova, Pavlina Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 87(2016)Supplement 1 Page Start: A91 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. I04 AAV5-MIHTT gene therapy demonstrates broad distribution and strong human mutant huntingtin lowering in a huntington disease minipig model. (September 2018) Authors: Klima, Jiri; Evers, Melvin M; Miniarikova, Jana; Juhas, Stefan; Vallès, Astrid; Bohuslavova, Bozena; Juhasova, Jana; Skalnikova, Helena Kupcova; Vodicka, Petr; Valekova, Ivona; Brouwers, Cynthia; Blits, Bas; Lubelski, Jacek; Kovarova, Hana; Deventer, Sander J van; Petry, Harald; Motlik, Jan; Kons... Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 89(2018)Supplement 1 Page Start: A89 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. I05 Sustained mutant huntingtin lowering in the brain and cerebrospinal fluid of huntington disease minipigs mediated by AAV5-MIHTT gene therapy. (September 2018) Authors: Valls, Astrid; Brouwers, Cynthia; Pintauro, Roberta; Snapper, Jolanda; Bohuslavova, Bozena; Sogorb-Gonzalez, Marina; Fodale, Valentina; Bresciani, Alberto; Ellederova, Zdenka; Blits, Bas; Motlik, Jan; Deventer, Sander van; Evers, Melvin; Konstantinova, Pavlina Journal: Journal of neurology, neurosurgery and psychiatry Issue: Volume 89(2018)Supplement 1 Page Start: A89 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. AAV mediated gene therapy as local treatment modality directed against amyloid beta oligomers in the brain using a high affinity, high specificity antibody: Nonhuman: Preclinical immunotherapeutic studies. (7th December 2020) Authors: Blits, Bas; Gouwenberg, Yvonne; Gebuis, Titia; van der Loo, Rolinka; van Kesteren, Ronald E.; Smit, August B.; Preusting, Hans; Scheefhals, Guus Journal: Alzheimer's & dementia Issue: Volume 16(2020)Supplement 9 Page Start: n/a Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗