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Author/Creator Balwani, Manisha

21. Pregnancy outcome in women with Gaucher disease type 1 who had unplanned pregnancies during eliglustat clinical trials. Issue 1 (18th October 2020)

Authors:
Lukina, Elena; Balwani, Manisha; Belmatoug, Nadia; Watman, Nora; Hughes, Derralynn; Gaemers, Sebastiaan J. M.; Foster, Meredith C.; Lewis, Grace; Peterschmitt, M. Judith
Journal:
JIMD reports
Issue:
Volume 57:Issue 1(2021)
Page Start:
76
Record Type:
Journal Article
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22. Real‐world effectiveness of eliglustat in treatment‐naïve and switch patients enrolled in the International Collaborative Gaucher Group Gaucher Registry. Issue 9 (24th June 2020)

Authors:
Mistry, Pramod K.; Balwani, Manisha; Charrow, Joel; Kishnani, Priya; Niederau, Claus; Underhill, Lisa H.; McClain, Monica R.
Journal:
American journal of hematology
Issue:
Volume 95:Issue 9(2020:Sep.)
Page Start:
1038
Record Type:
Journal Article
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23. Reply to: "Could Blood Hexosylsphingosine Be a Marker for Parkinson's Disease Linked with GBA1 Mutations"?. Issue 8 (18th August 2022)

Authors:
Surface, Matthew; Balwani, Manisha; Waters, Cheryl; Haimovich, Alexander; Gan‐Or, Ziv; Marder, Karen S.; Hsieh, Tammy; Song, Linxia; Padmanabhan, Shalini; Hsieh, Frank; Merchant, Kalpana M.; Alcalay, Roy N.
Journal:
Movement disorders
Issue:
Volume 37:Issue 8(2022)
Page Start:
1782
Record Type:
Journal Article
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24. Reply to: No Evidence that Glucosylsphingosine Is a Biomarker for Parkinson Disease. Issue 3 (29th January 2022)

Authors:
Surface, Matthew; Balwani, Manisha; Waters, Cheryl; Haimovich, Alexander; Gan‐Or, Ziv; Marder, Karen S.; Hsieh, Tammy; Song, Linxia; Padmanabhan, Shalini; Hsieh, Frank; Merchant, Kalpana M.; Alcalay, Roy N.
Journal:
Movement disorders
Issue:
Volume 37:Issue 3(2022)
Page Start:
654
Record Type:
Journal Article
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26. S1063 Disease Burden in Patients With Acute Hepatic Porphyria: Experience From the Phase 3 ENVISION Study. (October 2021)

Authors:
Wang, Bruce; Ventura, Paolo; Takase, Kei-ichiro; Thapar, Manish; Cassiman, David M.; Kubisch, Ilja; Hua, Zhaowei; Sweetser, Marianne T.; Balwani, Manisha
Journal:
American journal of gastroenterology
Issue:
Volume 116:Supplement(2021)ACG Annual Meeting Abstracts 1
Page Start:
S504
Record Type:
Journal Article
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27. S1154 Clinical Outcomes in Patients With Acute Hepatic Porphyria Treated With Givosiran Who Stopped Hemin Prophylaxis at Study Entry: A Post Hoc Analysis of Data From the Phase 3 ENVISION Study Through Month 12. (October 2020)

Authors:
Bonkovsky, Herbert L.; Balwani, Manisha; Sardh, Eliane; Gouya, Laurent; Rees, David C.; Stein, Penelope; Stölzel, Ulrich; Peiro, Paula Aguilera; Bissell, D. Montgomery; Keel, Sioban; Parker, Charles; Silver, Samuel; Windyga, Jerzy; D'Avola, Delia; Ross, Gayle; Stewart, Peter; Ritchie, Bruce; Oh, ...
Journal:
American journal of gastroenterology
Issue:
Volume 115:Supplement(2020)ACG Annual Meeting Abstracts 1
Page Start:
S578
Record Type:
Journal Article
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28. S1169 Twelve-Month Interim Analysis of Efficacy and Safety of Givosiran, an Investigational RNAi Therapeutic for Acute Hepatic Porphyria, in the ENVISION Open Label Extension. (October 2020)

Authors:
Sardh, Eliane; Balwani, Manisha; Rees, David C.; Stein, Penelope; Stölzel, Ulrich; Peiro, Paula Aguilera; Bissell, D. Montgomery; Bonkovsky, Herbert L.; Keel, Sioban; Parker, Charles; Phillips, John D.; Silver, Samuel; Windyga, Jerzy; D'Avola, Delia; Ross, Gayle; Stewart, Peter; Ritchie, Bruce; H...
Journal:
American journal of gastroenterology
Issue:
Volume 115:Supplement(2020)ACG Annual Meeting Abstracts 1
Page Start:
S584
Record Type:
Journal Article
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30. Transformation in pretreatment manifestations of Gaucher disease type 1 during two decades of alglucerase/imiglucerase enzyme replacement therapy in the International Collaborative Gaucher Group (ICGG) Gaucher Registry. Issue 9 (7th July 2017)

Authors:
Mistry, Pramod K.; Batista, Julie L.; Andersson, Hans C.; Balwani, Manisha; Burrow, Thomas Andrew; Charrow, Joel; Kaplan, Paige; Khan, Aneal; Kishnani, Priya S.; Kolodny, Edwin H.; Rosenbloom, Barry; Scott, C. Ronald; Weinreb, Neal
Journal:
American journal of hematology
Issue:
Volume 92:Issue 9(2017:Sep.)
Page Start:
929
Record Type:
Journal Article
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