1. Effectiveness of enzyme replacement therapy in adults with late‐onset Pompe disease: results from the NCS‐LSD cohort study. Issue 6 (7th June 2014) Authors: Anderson, L. J.; Henley, W.; Wyatt, K. M.; Nikolaou, V.; Waldek, S.; Hughes, D. A.; Lachmann, R. H.; Logan, S. Journal: Journal of inherited metabolic disease Issue: Volume 37:Issue 6(2014) Page Start: 945 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. Long‐term effectiveness of enzyme replacement therapy in adults with Gaucher disease: results from the NCS‐LSD cohort study. Issue 6 (11th February 2014) Authors: Anderson, L. J.; Henley, W.; Wyatt, K. M.; Nikolaou, V.; Hughes, D. A.; Waldek, S.; Logan, S. Journal: Journal of inherited metabolic disease Issue: Volume 37:Issue 6(2014) Page Start: 953 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
3. Long‐term effectiveness of enzyme replacement therapy in children with Gaucher disease: results from the NCS‐LSD cohort study. Issue 6 (18th March 2014) Authors: Anderson, L. J.; Henley, W.; Wyatt, K. M.; Nikolaou, V.; Waldek, S.; Hughes, D. A.; Pastores, G. M.; Logan, S. Journal: Journal of inherited metabolic disease Issue: Volume 37:Issue 6(2014) Page Start: 961 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
4. Long‐term effectiveness of enzyme replacement therapy in Fabry disease: results from the NCS‐LSD cohort study. Issue 6 (15th May 2014) Authors: Anderson, L. J.; Wyatt, K. M.; Henley, W.; Nikolaou, V.; Waldek, S.; Hughes, D. A.; Pastores, G. M.; Logan, S. Journal: Journal of inherited metabolic disease Issue: Volume 37:Issue 6(2014) Page Start: 969 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
5. The NCS‐LSD cohort study: a description of the methods and analyses used to assess the long‐term effectiveness of enzyme replacement therapy and substrate reduction therapy in patients with lysosomal storage disorders. Issue 6 (12th February 2014) Authors: Henley, W. E.; Anderson, L. J.; Wyatt, K. M.; Nikolaou, V.; Anderson, R.; Logan, S. Journal: Journal of inherited metabolic disease Issue: Volume 37:Issue 6(2014) Page Start: 939 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗