1. P112: ENERGIZE AND ENERGIZE-T: TWO PHASE 3, RANDOMIZED, DOUBLE-BLIND, PLACEBO-CONTROLLED STUDIES OF MITAPIVAT IN ADULTS WITH NON--TRANSFUSION-DEPENDENT OR TRANSFUSION-DEPENDENT ALPHA- OR BETA-THALASSEMIA. (31st January 2022) Authors: Kuo, K; Layton, D; Al-Samkari, H; Kattamis, A; Sheth, S; Taher, A; Viprakasit, V; Chamberlain, C; Czapla, L; Gheuens, S; Lynch, M; Tong, B; Uhlig, K; Cappellini, M Journal: HemaSphere Issue: Volume 6(2022)Supplement 1 Page Start: 23 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗
2. S116: LONG-TERM EFFICACY AND SAFETY OF THE ORAL PYRUVATE KINASE ACTIVATOR MITAPIVAT IN ADULTS WITH NON—TRANSFUSION-DEPENDENT ALPHA- OR BETA-THALASSEMIA. (31st January 2022) Authors: Kuo, K; Layton, D; Lal, A; Al-Samkari, H; Bhatia, J; Kosinski, P; Tong, B; Lynch, M; Uhlig, K; Vichinsky, E Journal: HemaSphere Issue: Volume 6(2022)Supplement 1 Page Start: 8 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗