1. Systemic messenger RNA as an etiological treatment for acute intermittent porphyria. (December 2018) Authors: Jiang, Lei; Berraondo, Pedro; Jericó, Daniel; Guey, Lin; Sampedro, Ana; Frassetto, Andrea; Benenato, Kerry; Burke, Kristine; Santamaría, Eva; Alegre, Manuel; Pejenaute, Álvaro; Kalariya, Mayur; Butcher, William; Park, Ji-Sun; Zhu, Xuling; Sabnis, Staci; Kumarasinghe, E.; Salerno, Timothy; Kenney,... Journal: Nature medicine Issue: Volume 24:Number 12(2018) Page Start: 1899 Record Type: Journal Article View Content: Available online (eLD content is only available in our Reading Rooms) ↗